Vol 2, No 1 (2015)

Table of Contents

Rare diseases policy

The use of animal models in disease research
Augusto Vitale, Flavia Chiarotti, Enrico Alleva
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1-4
A standard of care for the ultra-rare Marshall-Smith syndrome - developmental process and lessons learned
Ildikó Vajda, Sonja Bracke
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5-10

Guidelines, systematic reviews, health technology assessment, and horizon scanning

Report of an international workshop to explore the utility of the AGREE II instrument for appraisal of rare disease guidelines
Michele Hilton Boon, Jenny Harbour, Karen Ritchie, Lorna Thompson
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11-15