Author Details

Stockler, Sylvia, Treatable Intellectual Disability Endeavor in British Columbia (TIDE-BC), Division of Biochemical Diseases, Department of Pediatrics, BC Children’s Hospital, Child & Family Research Institute, University of British Columbia, Canada

  • Vol 1, No 2 (2014) - Rare diseases policy
    Bone marrow transplant for a boy with alpha-mannosidosis illustrates a family’s decision-making in rare diseases
    Abstract  PDF