Vallance, Hilary, Treatable Intellectual Disability Endeavor in British Columbia (TIDE-BC), Centre for Molecular Medicine and Therapeutics, British Columbia Children's Hospital, University of British Columbia, Canada
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Vol 1, No 2 (2014) - Rare diseases policy
Bone marrow transplant for a boy with alpha-mannosidosis illustrates a family’s decision-making in rare diseases
Abstract PDF