Stockler, Sylvia, Treatable Intellectual Disability Endeavor in British Columbia (TIDE-BC), Division of Biochemical Diseases, Department of Pediatrics, BC Children’s Hospital, Child & Family Research Institute, University of British Columbia, Canada
-
Vol 1, No 2 (2014) - Rare diseases policy
Bone marrow transplant for a boy with alpha-mannosidosis illustrates a family’s decision-making in rare diseases
Abstract PDF